Onasemnogene Abeparvovec 治疗脊髓性肌萎缩后坏死性小肠结肠炎 : 病例系列。
Mesh : Infant Female Infant, Newborn Humans Enterocolitis, Necrotizing / diagnosis etiology therapy Genetic Therapy Infant, Premature Muscular Atrophy, Spinal / genetics Infant, Newborn, Diseases / therapy Fetal Diseases Spinal Muscular Atrophies of Childhood / therapy
来 源: DOI:10.1016/j.jpeds.2023.113493