{Reference Type}: Journal Article
{Title}: Necrotizing Enterocolitis following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series.
{Author}: Gaillard J;Gu AR;Neil Knierbein EE;
{Journal}: J Pediatr
{Volume}: 260
{Issue}: 0
{Year}: 2023 09 19
{Factor}: 6.314
{DOI}: 10.1016/j.jpeds.2023.113493
{Abstract}: Onasemnogene abeparvovec treats spinal muscular atrophy by delivering a functional SMN1 gene. Necrotizing enterocolitis typically occurs in preterm infants. We report 2 term infants diagnosed with spinal muscular atrophy who presented with necrotizing enterocolitis after onasemnogene abeparvovec infusion. We discuss potential etiologies and propose monitoring for necrotizing enterocolitis after onasemnogene abeparvovec therapy.