[Nusinersen 治疗 4 例症状前脊髓性肌萎缩症] 。
Mesh : Humans Male Female Infant Child, Preschool Muscular Atrophy, Spinal / therapy diagnosis genetics drug therapy Spinal Muscular Atrophies of Childhood / therapy genetics diagnosis drug therapy Survival of Motor Neuron 2 Protein / genetics Child Exons Oligonucleotides
来 源: DOI:10.3760/cma.j.cn112140-20240307-00159