从具有 ATXN3 突变的 14 / 63 CAG 重复的志愿者的外周血单核细胞中建立人诱导的多能干细胞 GZHMCi0011 - A 。
Mesh : Humans Induced Pluripotent Stem Cells / metabolism Leukocytes, Mononuclear / metabolism Ataxin-3 / genetics metabolism Machado-Joseph Disease / genetics metabolism Mutation / genetics Volunteers Repressor Proteins / genetics
来 源: DOI:10.1016/j.scr.2023.103190