随着时间的推移 , CFSPID 病例中个性化医疗的创新策略。
关键词: CFTR modulators N = 1 clinical trials Organoids
Mesh : Child Humans Infant, Newborn Cystic Fibrosis / genetics therapy diagnosis Precision Medicine Mutation Neonatal Screening Cystic Fibrosis Transmembrane Conductance Regulator / genetics
来 源: DOI:10.1016/j.prrv.2023.06.001