成功的造血细胞移植治疗婴儿原发性骨髓纤维化 / VPS45 缺乏症 : 病例报告和文献复习。
Mesh : Humans Primary Myelofibrosis / diagnosis genetics therapy Hematopoietic Stem Cell Transplantation Neutropenia Congenital Bone Marrow Failure Syndromes Transplantation Conditioning Vesicular Transport Proteins
来 源: DOI:10.1007/s10875-023-01467-x