超微疾病的基因治疗 : 遗传学家的观点。
关键词: Adeno-associated viral vector Gene therapy Lentiviral vector Ultrarare
Mesh : Genetic Therapy / methods Humans Hematopoietic Stem Cell Transplantation Dependovirus / genetics Genetic Vectors Genetic Diseases, Inborn / therapy genetics Rare Diseases / therapy genetics Lentivirus / genetics
来 源:
DOI:10.1186/s12929-024-01070-1
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