Report From the Second Global Scientific Conference on Clinical Trial Design and Outcome Measures for RDH12-Associated Inherited Retinal Degeneration.

关于 RDH12 相关遗传性视网膜变性的临床试验设计和结果测量的第二届全球科学会议的报告。

• 影响指数: 3.048
• 发表时间: 2024 Aug 1
• 来源期刊: Transl Vis Sci Technol
• DOI: 10.1167/tvst.13.8.17
• PMID: 39120885
• 文章类型: Congress
• 中科院分区: Q4
• 方向: 医学
• 作者列表: Cerolini S,Bennett J,Leroy BP,Durham T,Coates C,Pletcher MT,Lacey S,Aleman TS

Mesh: Humans; Alcohol Oxidoreductases / genetics metabolism; Clinical Trials as Topic; Outcome Assessment, Health Care; Research Design; Retinal Degeneration / genetics therapy

Abstract

UNASSIGNED: A multi-stakeholder, patient centric approach will be critical to the design of future successful clinical trials with outcome measures relevant to the RDH12-IRD population.

摘要

■多方利益相关者，以患者为中心的方法对于设计与RDH12-IRD人群相关的结局指标的未来成功临床试验至关重要.