Abstract：
The rich history surrounding Diamond-Blackfan anaemia (DBA), originally described in 1938 as congenital hypoplastic anaemia2 reflects the evolution of paediatric haematology. In their paper, the authors1 present the results of a clinical trial using the thrombopoietin-mimetic agent eltrombopag to treat red cell failure in DBA. A low response rate belies the importance of this work. Commentary on: Duncan et al. Treatment of refractory/relapsed Diamond-Blackfan anaemia with eltrombopag. Br J Haematol 2024;204:2077-2085.
摘要：
钻石黑风扇贫血（DBA）的丰富历史，最初在1938年被描述为先天性发育不良2反映了儿科血液学的演变。在他们的论文中,作者1介绍了一项使用血小板生成素模拟剂eltrombopag治疗DBA中红细胞衰竭的临床试验结果.低回复率掩盖了这项工作的重要性。评论：邓肯等人。艾曲波帕治疗难治性/复发性Diamond-Blackfan贫血。BrJHaematol2024；204：2077-2085。
