关键词: CFTR correctors folding-defective proteins myogenic cells myotubes protein folding correctors proteostasis regulators sarcoglycanopathy
Mesh : Aminopyridines / pharmacology Benzodioxoles / pharmacology Cystic Fibrosis Cystic Fibrosis Transmembrane Conductance Regulator / genetics metabolism Drug Combinations HEK293 Cells Humans Muscle Fibers, Skeletal / drug effects metabolism Mutation Proteasome Endopeptidase Complex / drug effects Sarcoglycanopathies / drug therapy genetics metabolism pathology Sarcoglycans / genetics metabolism
来 源:
DOI:10.3390/ijms21051813
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