遗传性视网膜疾病的治疗进展 : 早期视网膜下基因治疗临床试验和未来计划的候选人。
关键词: ABCA4 BCM CNGA3 CNGB3 Gene therapy Genetic retinal degenerations Leber congenital amaurosis MERTK MYO7A Molecular mechanisms NPHP5 OPN1LW OPN1MW PDE6B REP1 RLBP1 RPE65 RPGR RPGRIP1 Retinitis pigmentosa TULP1
Mesh : Clinical Trials as Topic Eye Diseases, Hereditary / therapy Gene Transfer Techniques Genetic Therapy / methods Humans Leber Congenital Amaurosis / therapy Retinal Degeneration / therapy Retinitis Pigmentosa / therapy
来 源:
DOI:10.1016/j.preteyeres.2019.100827
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