关键词: Drépanocytose Gene therapy Greffe de cellules souches hématopoïétiques Hematopoietic stem cell transplantation Hydroxyurea Hydroxyurée Red blood cell transfusion Sickle cell disease Thalassemia Thalassémie Thérapie génique Transfusion érythrocytaire
Mesh : Allografts Anemia, Sickle Cell / drug therapy therapy Child Emergencies Erythrocyte Transfusion Exchange Transfusion, Whole Blood Genetic Therapy Hematopoietic Stem Cell Transplantation Hemoglobinopathies / therapy Humans Hydroxyurea / therapeutic use Multiple Organ Failure / therapy Thalassemia / therapy
来 源:
DOI:10.1016/j.tracli.2019.06.323
PDF(Sci-hub)