关键词: DFNB9 deafness dual AAV gene therapy otoferlin
Mesh : Animals Deafness / genetics therapy Dependovirus / genetics Disease Models, Animal Genetic Therapy Genetic Vectors Humans Membrane Proteins / genetics Mice Mice, Inbred C57BL Mice, Transgenic
来 源:
DOI:10.1073/pnas.1817537116
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